Musculoskeletal Diseases
Jul 27, 2020| Posted in: Congenital And Genetic Conditions, Drug Development, Musculoskeletal Diseases, Neurology/Nervous System Diseases, News
Diego Cadavid, MD of Fulcrum Therapeutics provides an…
Update on the Phase 2 Facioscapulohumeral Muscular Dystrophy Clinical Trial
Jul 21, 2020| Posted in: Congenital And Genetic Conditions, Drug Development, Musculoskeletal Diseases, Neurology/Nervous System Diseases, News
Diego Cadavid, MD, of Fulcrum Therapeutics summarizes the…
Research Presented at AAN 2020 Show Promise for FSHD Treatment
Jul 5, 2020| Posted in: Diagnosis, Gastrointestinal Diseases, Musculoskeletal Diseases, Neurology/Nervous System Diseases, Ophthalmology/Eye Diseases
Bruce Cree, MD of the University of California…
Tips for Diagnosing Neuromyelitis Optica Spectrum Disorder (NMOSD)
Jun 26, 2020| Posted in: Autoimmune / Autoinflammatory Disorders, Drug Development, Musculoskeletal Diseases, Neurology/Nervous System Diseases, News, Regulations, Treatment
The U.S. Food and Drug Administration has approved…
FDA Approves Fenfluramine to Reduce Seizures in Children with Dravet Syndrome
Jun 23, 2020| Posted in: Autoimmune / Autoinflammatory Disorders, Musculoskeletal Diseases, Neurology/Nervous System Diseases, Ophthalmology/Eye Diseases
Kathleen Hawker, MD at Genentech describes two abstracts…
New Studies Show Continued Benefit of Satralizumab to Treat NMOSD
Jun 19, 2020| Posted in: Cancers, Musculoskeletal Diseases, News, Regulations, Treatment
The US Food and Drug Administration (FDA) has…
FDA Approves Burosumab To Treat Tumor-induced Osteomalacia
Jun 17, 2020| Posted in: Autoimmune / Autoinflammatory Disorders, Kidney And Urinary Diseases, Musculoskeletal Diseases, News, Regulations, Treatment
The U.S. Food and Drug Administration (FDA) has approved…
FDA Approves First Drug to Treat Still’s Disease
May 21, 2020| Posted in: Musculoskeletal Diseases
Duchenne muscular dystrophy (DMD) is a progressive form of…
Duchenne Muscular Dystrophy
May 20, 2020| Posted in: Congenital And Genetic Conditions, Metabolic Disorders, Musculoskeletal Diseases
Heather A. Lau, MD, Director, Lysosomal Storage Disease…
Overview of the Mucopolysaccharidoses
May 7, 2020| Posted in: Congenital And Genetic Conditions, Expert Perspectives, Musculoskeletal Diseases
Michael Snape, PhD, Chief Scientific Officer at AMO…
Congenital Myotonic Dystrophy
