Musculoskeletal Diseases

Oct 15, 2020| Posted in: Congenital And Genetic Conditions, Endocrine Disorders, Expert Perspectives, Kidney And Urinary Diseases, Musculoskeletal Diseases, Treatment

Approval of Burosumab-twza for Treating Tumor-Induced Osteomalacia

Erik Harris, Executive Vice President and Chief Commercial…

Oct 14, 2020| Posted in: Congenital And Genetic Conditions, Musculoskeletal Diseases, Neurology/Nervous System Diseases

SMA Adult Talks About His Diagnostic Journey

Jim Willson, a patient with spinal muscular atrophy…

Oct 5, 2020| Posted in: Advocacy, Congenital And Genetic Conditions, Heart Diseases, Musculoskeletal Diseases, Neurology/Nervous System Diseases, Ophthalmology/Eye Diseases

Video Game Tournament Provides Support for Duchenne Patients

Tiffany Cook, Family Resource Manager of CureDuchenne, discusses…

Sep 16, 2020| Posted in: Congenital And Genetic Conditions, Expert Perspectives, Heart Diseases, Lysosomal Storage Disorders, Metabolic Disorders, Musculoskeletal Diseases, Neurology/Nervous System Diseases, Ophthalmology/Eye Diseases

New CME/CE focused on Mucopolysaccharidosis I (MPS I)

In this 4 module CME/CE program, hosted by…

Sep 14, 2020| Posted in: Congenital And Genetic Conditions, Expert Perspectives, Metabolic Disorders, Musculoskeletal Diseases, Ophthalmology/Eye Diseases, Treatment

How Rare Disease Treatments Get Approved

Emil Kakkis, MD, President and Founder of Ultragenyx…

Sep 10, 2020| Posted in: Drug Development, Expert Perspectives, Musculoskeletal Diseases, Treatment

Treatment Options for Tenosynovial Giant Cell Tumors

Howard Rutman, MD, vice president of medical affairs…

Sep 1, 2020| Posted in: Cancers, Diagnosis, Musculoskeletal Diseases

The Diagnostic Journey for a TGCT Patient

Howard Rutman, MD, Vice President of Medical Affairs…

Aug 13, 2020| Posted in: Cancers, Drug Development, Musculoskeletal Diseases

Tenosynovial Giant Cell Tumors (TGCT) Explained

Howard Rutman, MD from Daiichi Sankyo talks about…

Aug 13, 2020| Posted in: Musculoskeletal Diseases, News, Regulations, Treatment

FDA Approves Second Drug to Treat DMD Patients Amenable to Exon 53 Skipping

The U.S. Food and Drug Administration (FDA) has…

Aug 4, 2020| Posted in: Cancers, Diagnosis, Musculoskeletal Diseases, Treatment

Imaging and Tumor-Induced Osteomalacia

Peter Tebben, MD, of the Mayo Clinic in…

CME Program: Mucopolysaccharidoses (MPSs) Highlights from WORLDSymposium 2020

Barbara K. Burton, MD highlights the latest information about MPSs from WORLDSymposium and provides expert analysis of its clinical relevance for members of the care team in order to help them care for patients with these rare diseases.

Rare Disease Clinical Trials CME Program

Learn about clinical trials and rare diseases through these brief courses that are certified for CME and CNE credit.

Heather Lau, MD, MS, NYU School of Medicine, New York, NY
Morie A Gertz, MD, Mayo Clinic, Rochester, MN
Timothy Craig, DO, Penn State University, Hershey, PA
Eric T. Wong, MD, Harvard Medical School, Boston, MA

Musculoskeletal Diseases

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