Musculoskeletal Diseases

Jun 19, 2020| Posted in: Cancers, Musculoskeletal Diseases, News, Regulations, Treatment

FDA Approves Burosumab To Treat Tumor-induced Osteomalacia

The US Food and Drug Administration (FDA) has…
May 21, 2020| Posted in: Musculoskeletal Diseases

Duchenne Muscular Dystrophy

Duchenne muscular dystrophy (DMD) is a progressive form of…
May 20, 2020| Posted in: Congenital And Genetic Conditions, Metabolic Disorders, Musculoskeletal Diseases

Overview of the Mucopolysaccharidoses

Heather A. Lau, MD, Director, Lysosomal Storage Disease…
May 7, 2020| Posted in: Congenital And Genetic Conditions, Expert Perspectives, Musculoskeletal Diseases

Congenital Myotonic Dystrophy

Michael Snape, PhD, Chief Scientific Officer at AMO…

CME Program: Mucopolysaccharidoses (MPSs) Highlights from WORLDSymposium 2020

Barbara K. Burton, MD highlights the latest information about MPSs from WORLDSymposium and provides expert analysis of its clinical relevance for members of the care team in order to help them care for patients with these rare diseases.

Rare Disease Clinical Trials CME Program

Learn about clinical trials and rare diseases through these brief courses that are certified for CME and CNE credit.
  • Heather Lau, MD, MS, NYU School of Medicine, New York, NY
  • Morie A Gertz, MD, Mayo Clinic, Rochester, MN
  • Timothy Craig, DO, Penn State University, Hershey, PA
  • Eric T. Wong, MD, Harvard Medical School, Boston, MA

Musculoskeletal Diseases


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