Expert Perspectives
Jan 19, 2021| Posted in: Cancers, Drug Development, Hematologic Disorders, Treatment
Janssen Initiates Rolling Submission to FDA for cilta-cel to Treat Relapsed/Refractory Multiple Myeloma
Mark Wildgust, PhD, Vice President, Oncology Global Media… Jan 19, 2021| Posted in: Endocrine Disorders, Ophthalmology/Eye Diseases
Treating Thyroid Eye Disease with Tepezza
Elizabeth Thompson, PhD at Horizon Therapeutics shares details… Jan 18, 2021| Posted in: Congenital And Genetic Conditions, Drug Development, Heart Diseases, Treatment
Treatment Options for HoFH
James Underberg, MD, Clinical Assistant Professor of Medicine… Jan 18, 2021| Posted in: Congenital And Genetic Conditions, Diagnosis, Lysosomal Storage Disorders, Metabolic Disorders, Neurology/Nervous System Diseases
Diagnosing Niemann-Pick Type C
Elizabeth Berry-Kravis, MD, PhD, co-director of the Molecular… Jan 18, 2021| Posted in: Congenital And Genetic Conditions, Drug Development, Musculoskeletal Diseases, Skin Conditions
Ipsen Biopharmaceuticals Commitment to Fibrodysplasia Ossificans Progressiva (FOP)
Stephanie Brown, the SVP of rare diseases at… Jan 17, 2021| Posted in: Advocacy, Congenital And Genetic Conditions, Musculoskeletal Diseases, Treatment
Treating Infantile-Onset Facioscapulohumeral Muscular Dystrophy
Ally Roets and her son Sam — who… Jan 17, 2021| Posted in: Cancers, Hematologic Disorders, Treatment
Overview of ECHELON-1 Study for Hodgkin Lymphoma
Dr. Anna Sureda, Head of the Onco-Hematology Service… Jan 16, 2021| Posted in: Endocrine Disorders, Ophthalmology/Eye Diseases
Diagnostic Challenges of Thyroid Eye Disease
Elizabeth Thompson, PhD at Horizon Therapeutics discusses the… Jan 15, 2021| Posted in: Congenital And Genetic Conditions, Drug Development, Musculoskeletal Diseases, Skin Conditions
Ipsen Biopharmaceuticals Patient-Focused Approach to Rare Diseases
Stephanie Brown, the SVP of rare diseases at… Jan 15, 2021| Posted in: Congenital And Genetic Conditions, Diagnosis, Lysosomal Storage Disorders, Metabolic Disorders, Neurology/Nervous System Diseases