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Join Professors João Gonçalves and Paolo Calicaeti in this educational webinar discussing how PEGylation represents a major technological advancement in the development and optimization of therapeutic proteins.
...https://checkrare.com/optimizing-therapeutic-proteins-through-pegylation/
#CheckRare #RareDisease #lysosomal #RareLysosomal
Optimizing Therapeutic Proteins Through PEGylation: Key Parameters and Impacts (Full Program)
What Is PEGylation and Why Is It Important? (Chapter 1)
Biopharmaceutical and Immunological Properties of PEGylated Proteins (Chapter 2)
Chemical Conjugation of PEG (Chapter 3)
Factors Influencing Immunogenicity in Pegylated Therapeutics (Chapter 4)
Marina Kremyanskaya, MD, PhD, Icahn School of Medicine at Mount Sinai, discusses the development of gene silencer divesiran for treatment of polycythemia vera (PV).
https://checkrare.com/development-of-gene-silencer-for-treatment-of-polycythemia-vera/
📣 Stay up to date on the most recent FDA approvals and PDUFA dates in the rare disease space with our 2025 Orphan Drugs webpage!
https://checkrare.com/2025-orphan-drugs-pdufa-dates-and-fda-approvals/
#CheckRare #RareDiseases #PDUFADates #FDAApproval
This CME program, hosted by John Kuruvilla, MD, explores best practices for discussing possible clinical trial participation with patients who have hematologic malignancies.
#CheckRare #CME
WHIM Syndrome: Overview, Diagnosis, and Magement
WHIM Syndrome: Overview and Importance of Early Diagnosis (Chapter 1)
Managing WHIM Syndrome (Chapter 2)
This CME program, hosted by Richard J. Nowak, MD, MS, explains the role of neonatal fragment crystallizable receptor (FcRn) in myasthenia gravis (MG) and how treatments that target FcRn are being used to manage patients with MG.
#CheckRare #CME #MyastheniaGravis
Larisa Geskin, MD, Columbia University Medical Center, discusses the challenges of diagnosing cutaneous T-cell lymphoma.
#CheckRare #RareDisease #CTCL
https://checkrare.com/ctcl-the-role-of-dermatologists-in-diagnosing-and-caring-for-patients/
Gaucher Community Alliance
This CME program, developed by Howard Trachtman, MD, and Carla M. Nester, MD, addresses the complexities involved in diagnosing, treating, and managing patients with various complement-mediated kidney disorders, such as C3 glomerulopathy and atypical hemolytic uremic syndrome (aHUS).
...#CheckRare #CME #RareDisease #KidneyDisorders
Citizen Health: AI-Powered Platform for Rare Conditions
CheckRare is delighted to once again be covering #ASH2024
#CheckRare #RareDisease
Rates of Severe Neutropenia and Infection Risk in Patients Treated With Deferiprone
CheckRare November 1, 2024 10:11 am