Living with Charcot-Marie-Tooth Disease

Charcot-Marie-Tooth disease (CMT) is one of the most common inherited neurological disorders, affecting approximately 1 in 2,500 people in the United States. The disease is named for the three physicians who first identified it in 1886 – Jean-Martin Charcot and...

How Ovid Therapeutics Works With Patient Groups

Amit Rakhit, MD, Chief Medical and Portfolio Officer at Ovid Therapeutics, discusses how his company values working with patient groups. Ovid Therapeutics is a biopharmaceutical company focused exclusively on developing impactful medicines for patients and families...

The MOA of Senicapoc: A Gardos Channel Blocker

Lara Sullivan, MD, President and Founder at SpringWorks Therapeutics discusses the mechanism of action of Senicapoc (a Gardos channel blocker), an emerging treatment for Hereditary Xerocytosis, a genetic disorder in which red blood cells become dehydrated due to loss...

Still’s Disease Overview

Len Walt, Vice President, Head of Medical Affairs, Sobi in North America, provides an overview of Still’s disease, a rare inflammatory disorder that affects the entire body (systemic disease). Still’s disease, a disorder featuring inflammation, is...

Resources Available for Patients Suffering from Polycythemia Vera

David Gelly is a patient with Polycythemia Vera (PV). In this interview he discusses some of the resources available to patients with this rare condition, including Voices of MPN. PVs are a group of rare blood cancers called Myeloproliferative Neoplasms (MPNs). MPNs...
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