Treatment

May 28, 2020| Posted in: News, Regulations, Treatment

FDA Approves Drug to Treat Malaria

The  U.S. Food and Drug Administration (FDA) has…
May 26, 2020| Posted in: Cancers, Hematologic Disorders, Treatment

Treatment of AML in the Elderly Has Changed Significantly

Courtney  DiNardo, MD, Associate Professor at the University…
May 25, 2020| Posted in: Cancers, News, Regulations, Treatment

FDA Approves New First-line Therapy for Rare Lung Cancer

The U.S. Food and Drug Administration (FDA) has…
May 22, 2020| Posted in: Cancers, Hematologic Disorders, Treatment

PTG-300 Showing Promise to Control Hemocrit Levels in Polycythemia Vera

Ronald Hoffman, MD at The Icahn School of Medicine…
May 21, 2020| Posted in: Cancers, Congenital And Genetic Conditions, News, Treatment

Data from Von-Hippel-Lindau Clinical Trial Shows Promise for HIF-2a Inhibitor

Eric Jonasch, MD, Professor, Department of Genitourinary Medical…
May 20, 2020| Posted in: Autoimmune / Autoinflammatory Disorders, Drug Development, News, Treatment

Can Boosting the Immune Response Help Treat COVID-19?

Dr. Gary Grohmann, Director of the Australian Immunisation…
May 19, 2020| Posted in: Cancers, Gastrointestinal Diseases, News, Regulations, Treatment

FDA Approves New Treatment for 4th-Line Treatment for GIST

The U.S. Food and Drug Administration (FDA) has…
May 18, 2020| Posted in: Cancers, News, Regulations, Skin Conditions, Treatment

FDA Approves New Drug for Kaposi Sarcoma

The U.S. Food and Drug Administration (FDA) has…

Rare Disease Clinical Trials CME Program

Learn about clinical trials and rare diseases through these brief courses that are certified for CME and CNE credit.
  • Heather Lau, MD, MS, NYU School of Medicine, New York, NY
  • Morie A Gertz, MD, Mayo Clinic, Rochester, MN
  • Timothy Craig, DO, Penn State University, Hershey, PA
  • Eric T. Wong, MD, Harvard Medical School, Boston, MA

WHIM Syndrome Learning Center

WHIM syndrome is a rare, congenital primary immunodeficiency disorder associated with severe neutropenia that affects all ages. However, due to the heterogeneous presentation of the disease, coupled with lack of awareness of the condition, the diagnosis may be delayed, sometimes even into adulthood.

CME Program: Gaucher Disease Highlights from WORLDSymposium 2020

Neal Weinreb, MD, FACP highlights the latest information about Gaucher disease from WORLDSymposium and provides expert analysis of its clinical relevance to help health care providers better care for patients with this rare disease.

CME Program: Fabry Disease Highlights from WORLDSymposium 2020

Ozlem Goker-Alpan, MD highlights the latest Fabry disease information from the WORLDSymposium and provides expert analysis of its clinical relevance for members of the care team in order to help them care for patients with this rare disease.

CME Program: Mucopolysaccharidoses (MPSs) Highlights from WORLDSymposium 2020

Barbara K. Burton, MD highlights the latest information about MPSs from WORLDSymposium and provides expert analysis of its clinical relevance for members of the care team in order to help them care for patients with these rare diseases.

Tenosynovial Giant Cell Tumor (TGCT)

Tenosynovial giant cell tumor (TGCT) is a non-malignant tumor involving the joint synovium, bursae, and tendon sheath. These rare tumors are sometimes referred to as giant cell tumor of the tendon sheath (GCT-TS) and/or pigmented villonodular synovitis (PVNS).

TTR Amyloidosis CME Program

Morie A Gertz, MD, MACP provides an overview of TTR Amyloidosis – including how to shorten individuals’ diagnostic journey and the time till they access treatment which might improve their quality of life or even prevent disease progression – through these brief courses that are certified for CME credit.

CME Program: Managing Individuals With Eosinophilic Granulomatosis with Polyangiitis (EGPA)

Michael E. Wechsler, MD, MMSc provides an overview of Eosinophilic Granulomatosis with Polyangiitis (EGPA) – including how to shorten individuals’ diagnostic journey and the time till they access effective therapy – through these brief courses that are certified for CME credit.

Spinal Muscular Atrophy CME Program

Nancy L. Kuntz, MD, FAAN discusses diagnosing and managing people with spinal muscular atrophy through these brief courses that are certified for CME and CNEcredit.

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