by Peter Ciszewski | Oct 20, 2020
J.G. Jones, comic book artist known for his work with D.C. and Marvel, discusses his journey with a myeloproliferative neoplasm (MPN). MPNs are rare, chronic blood cancers and can be classified based on the presence or absence of the Philadelphia chromosome....
by Peter Ciszewski | Oct 19, 2020
Mary Smith, PhD, senior vice president of clinical research and development at SpringWorks Therapeutics explains how nirogacestat works to treat individuals with Desmoid tumors. Desmoid tumors are benign tumors that can grow into surrounding healthy tissues,...
by Peter Ciszewski | Oct 19, 2020
Lisa Nachtigall MD, Clinical Director, Neuroendocrine and Pituitary Clinical Center at Massachusetts General Hospital, and Associate Professor at Harvard Medical School provides an overview of Acromegaly. Acromegaly is typically caused by a benign tumor in the...
by Peter Ciszewski | Oct 17, 2020
Joslyn Crowe, executive director of the National Niemann-Pick Disease Foundation (NNPDF), describes some of the different ways that parents cope with the news that their child has a rare, and often fatal, disease such as Niemann-Pick disease. Niemann Pick...
by Peter Ciszewski | Oct 15, 2020
Erik Harris, Executive Vice President and Chief Commercial Officer at Ultragenyx Pharmaceutical Inc. discusses the recent approval of burosumab-twza (Crysvita) for treatment of tumor-induced osteomalacia (TIO). TIO is a rare disease caused by typically benign,...
