2023 Orphan Drugs: PDUFA Dates and FDA Approvals

2025 Orphan Drugs: PDUFA Dates and FDA Approvals 2024 Orphan Drugs: PDUFA Dates and FDA Approvals 2023 Orphan Drugs: PDUFA Dates and FDA Approvals 2022 Orphan Drugs: PDUFA Dates and FDA Approvals 2021 Orphan Drugs: PDUFA Dates and FDA Approvals Rare diseases and...

Rett Syndrome Related Disorders

  Jeffrey L. Neul, MD, PhD, Director of the Vanderbilt Kennedy Center, and Professor of Pediatrics, Division of Neurology, Pharmacology, and Special Education, at the Vanderbilt University Medical Center, discusses disorders related to Rett syndrome that are also...