BCMA-targeted Therapies and Multiple Myeloma

Peter Voorhees, MD, of the Levine Cancer Institute in Charlotte NC discusses the emerging treatments for multiple myeloma that are focused on BCMA-targeted therapies. B Cell maturation antigen (BCMA) is a transmembrane glycoprotein expressed in significantly high...

Hemophilia A Treatment Options

  Snejana Krassova, MD of Bayer Pharmaceuticals talks about the need for more treatment options to be available for persons with hemophilia A. Hemophilia A is a genetic disorder caused by missing or defective factor VIII, a clotting protein. Symptoms will vary...

Surgery for Thyroid Eye Disease

  Gary Joseph Lelli, MD, of the Department of Ophthalmology at Weill Cornell Medicine discusses surgical options currently available to treat thyroid eye disease due to Graves’ disease. Graves’ disease is an immune system disorder that results in the...

Diagnosing AADC Deficiency

  Claudio Santos, MD, MBA, of PTC Therapeutics describe the pathophysiology of Aromatic l-amino acid decarboxylase (AADC) deficiency and how it is diagnosed. AADC deficiency is a rare genetic disorder due to mutations in the DDC gene that regulates the AADC...

FDA Approves Vaccine to Prevent Ebola Virus Disease

The U.S. Food and Drug Administration (FDA) has approved the first vaccine to prevent  Ebola virus disease. The vaccine, Ervedo, by Merck & Co, Inc, was granted approval based on a study conducted during the 2014-2016 outbreak in Guinea. The study involved 3,537...