by Peter Ciszewski | Dec 19, 2017
Len Walt, Vice President, Head of Medical Affairs, Sobi in North America, provides an overview of Still’s disease, a rare inflammatory disorder that affects the entire body (systemic disease). Still’s disease, a disorder featuring inflammation, is...
by Peter Ciszewski | Dec 19, 2017
Robert Derham, Founder of CheckOrphan, the longest running website focused exclusively on rare diseases and orphan drugs, discusses his unique web platform.
by Peter Ciszewski | Dec 12, 2017
Exciting news for the rare disease community: For the first time a therapy has been shown to slow the progression of Huntington’s disease, giving hopes to patients suffering from the terrible, incurable disorder. In what the Huntington’s Disease Society of...
by Peter Ciszewski | Dec 11, 2017
In four studies presented during the 59th American Society of Hematology (ASH) Annual Meeting and Exposition in Atlanta, researchers announce promising findings on innovative tools and therapies for hard-to-treat blood disorders including sickle cell disease (SCD),...
by Peter Ciszewski | Dec 11, 2017
Four studies presented at the 59th American Society of Hematology (ASH) Annual Meeting and Exposition in Atlanta highlight the multiple ways in which novel targeted cancer therapies are now being deployed to improve outcomes and quality of life for patients with rare,...
