by Peter Ciszewski | Nov 24, 2017
Melissa P. Wasserstein, MD, Chief of Pediatric Genetic Medicine at the Children’s Hospital at Montefiore, New York City, discusses the challenges of recruiting patients for rare disease clinical trials, including Nieman-Pick disease.
by Peter Ciszewski | Nov 24, 2017
Ellen Ritchie, MD, Associate Professor of Clinical Medicine, Weill Cornell Medical College, discusses the challenges of diagnosing Myeloproliferative Neoplasms (MPNs). MPNs are rare, chronic blood cancers. Chronic conditions last for a long period of time and may...
by Peter Ciszewski | Nov 24, 2017
David G. Birch, PhD, Chief Scientific and Executive Officer and Director of the Rose-Silverthorne Retinal Degenerations Laboratory, Retina Foundation of the Southwest discusses how patients suffering from X-Linked Retinoschisis (XLRS) are typically treated. X-linked...
by Peter Ciszewski | Nov 24, 2017
Philippe Maitre, Executive Vice President, US Operations for Onxeo discusses his company’s orphan oncology pipeline. The Company’s growth strategy is primarily driven by the development of its orphan oncology candidates which meet an established and unaddressed...
by Peter Ciszewski | Nov 24, 2017
Sandesh Seth discusses upcoming events of Actinium Pharmaceuticals, a clinical-stage biopharmaceutical company focused on developing and commercializing targeted therapies for safer myeloablation and conditioning of the bone marrow prior to a bone marrow transplant...