by CheckRare Staff | Feb 1, 2023
Ying Huang, PhD, CEO of Legend Biotech, discusses updated results from the CARTITUDE-1 study and data from two cohorts in the CARTITUDE-2 study. Both of these studies are evaluating cilta-cel in patients with relapsed/refractory multiple myeloma. These data...
by CheckRare Staff | Jan 31, 2023
Conditioning Agent (JSP191) For Stem Cell Transplants Shows Promise in Patients With Fanconi Anemia Ronald Martell, President, and CEO of Jasper Therapeutics, discusses the positive data from the ongoing phase 1/2 study testing JSP191 as a conditioning...
by CheckRare Staff | Jan 27, 2023
Adeline Vanderver, MD, Program Director of the Leukodystrophy Center in the Division of Neurology at Children’s Hospital of Philadelphia (CHOP), and Co-Principal Investigator of the Global Leukodystrophy Initiative Clinical Trials Network (GLIA-CTN), lists key...
by CheckRare Staff | Jan 26, 2023
« Prev1 / 1Next »WHIM Syndrome Full Panel DiscussionThe Importance of Early Diagnosis (WHIM Syndrome Panel Chapter 1)The Importance of Early Identification (WHIM Syndrome Panel Chapter 2)Burden of Disease With the Warts and HPV Disease (WHIM Syndrome Panel...
by CheckRare Staff | Jan 26, 2023
Diana Castro, MD, founder of the Neurology Rare Disease Center in Dallas, Texas discusses newborn screening for spinal muscular atrophy (SMA) in the United States. SMA is a genetic disease that affects motor neurons in the spinal cord and control of muscle...
