by Craig McCabe and James Radke, PhD | Jun 1, 2023
Jack Johnson, of the Fabry Support and Information Group (FSIG) talks about the different types of pain often associated with Fabry disease. Fabry disease is a rare, X-linked lysosomal storage disorder that is caused by the deficiency of the enzyme...
by Madaline Spencer and James Radke, PhD | May 30, 2023
Samiah Al-Zaidy, MD, Vice President of Clinical Development and Lead on the Passage Bio GM1 Gangliosidosis (GM1) Program, gives an overview of GM1. As Dr. Al-Zaidy explains, GM1 is an inherited lysosomal disorder caused by mutations in the GLB1 gene. These...
by James Radke, PhD | May 29, 2023
Kerry Mello-Parker, Director of Clinical Compliance for Rare & Complex Therapies, and Shanna Martin, Registered Nurse, from Shields Health Solutions, discuss the Risk Evaluation and Mitigation Strategies (REMS) program for macitentan, a treatment option for...
by James Radke, PhD | May 25, 2023
Kerry Mello-Parker, Director of Clinical Compliance for Rare & Complex Therapies, Shields Health Solutions, discusses the benefits of an integrated care model for high-risk diseases. As Ms. Mello-Parker explains, Shields Health Solutions works with a national...
by Madaline Spencer and James Radke, PhD | May 24, 2023
Shanna Martin, Registered Nurse from Shields Health Solutions, discusses common barriers clinicians face in managing patients with pulmonary arterial hypertension (PAH). PAH is a rare, progressive disorder characterized by high blood pressure (hypertension) in...
