Efficacy of Vosoritide to Treat Hypochondroplasia

Andrew Dauber, MD, MMsc, Chief of Endocrinology at Children’s National, discusses the efficacy of vosoritide to treat persons with hypochondroplasia.     Hypochondroplasia is a rare skeletal disease characterized by very short stature, similar to...

Efficacy of Infigratinib on Achondroplasia

Daniela Rogoff, MD, PhD, Chief Medical Officer, Skeletal Dysplasia of BridgeBio, discusses the efficacy of infigratinib to treat persons with achondroplasia.   Achondroplasia is a disorder of bone growth that prevents the changing of cartilage to bone,...