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Phase 2a GATEWAY Trial of PORT-77 in Patients With Erythropoietic Protoporphyria Shows Promise

by Madaline Spencer | Jul 31, 2026

Pete Schmidt, MD, MSc, Chief Medical Officer of Portal Therapeutics, discusses data from the phase 2a GATEWAY trial testingPORT-77, an ABCG2 inhibitor, in patients with erythropoietic protoporphyria (EPP).    EPP is a rare congenital metabolic disorder...

Patient Perspective: Diagnosis and Treatment Journey With ROS1-Positive Non-Small Cell Lung Cancer

by Madaline Spencer | Jul 30, 2026

Jim Herbert, a patient with ROS1-positive non-small cell lung cancer (NSCLC), discusses his diagnosis and treatment journey.     ROS1-positive NSCLC is a rare and aggressive lung cancer that typically occurs in patients aged 50 years and older and who have...

Results from the MajesTEC-9 and CARTITUDE-4 Clinical Trials in Patients With Relapsed/Refractory Multiple Myeloma

by Madaline Spencer | Jul 29, 2026

Roberto Mina, MD, Assistant Professor at Winship Cancer Institute at Emory University, discusses results from the MajesTEC-9 and CARTITUDE-4 clinical trials in patients with relapsed/refractory multiple myeloma (RRMM).     MM is a rare blood cancer...

Going Beyond Lab Values: Cognitive Impairment in Patients With Immune Thrombocytopenia

by Madaline Spencer | Jul 28, 2026

David Kuter, MD, DPhil, Director of Clinical Hematology at Massachusetts General Hospital and Professor of Medicine at Harvard Medical School, discusses cognitive impairment in patients with immune thrombocytopenia (ITP).     ITP is an autoimmune bleeding...

FDA Approves Jideytro (Zidesamtinib) for Adults With ROS1-Positive Non-Small Cell Lung Cancer

by Madaline Spencer | Jul 27, 2026

The US Food and Drug Administration (FDA) has approved Jideytro (zidesamtinib) for the treatment of adult patients with locally advanced or metastatic ROS1-positive non-small cell lung cancer (NSCLC) who have received a prior ROS1 kinase inhibitor. ROS1-positive NSCLC...
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