Endocrine Disorders

Oct 20, 2020| Posted in: Cancers, Diagnosis, Endocrine Disorders, Metabolic Disorders, Skin Conditions

Diagnostic Delays are Common for Acromegaly

Susan Samson, MD, PhD, of Baylor College of…

Oct 19, 2020| Posted in: Cancers, Endocrine Disorders, Metabolic Disorders, Skin Conditions

Acromegaly Overview

Lisa Nachtigall MD, Clinical Director, Neuroendocrine and Pituitary…

Oct 15, 2020| Posted in: Congenital And Genetic Conditions, Endocrine Disorders, Expert Perspectives, Kidney And Urinary Diseases, Musculoskeletal Diseases, Treatment

Approval of Burosumab-twza for Treating Tumor-Induced Osteomalacia

Erik Harris, Executive Vice President and Chief Commercial…

Oct 14, 2020| Posted in: Cancers, Endocrine Disorders, Metabolic Disorders, Treatment

Treatment Options for Acromegaly

Susan Samson, MD, PhD, of Baylor College of…

Oct 1, 2020| Posted in: Congenital And Genetic Conditions, Drug Development, Endocrine Disorders, Neurology/Nervous System Diseases, Treatment

Gene Therapy Shows Promise for Cerebral Adrenoleukodystrophy (CALD)

Jörn-Sven Kühl, MD, Department of Pediatric Oncology, Hematology…

Jul 6, 2020| Posted in: Cancers, Endocrine Disorders, Metabolic Disorders, Regulations, Treatment

New Oral Octreotide Approved to Treat Acromegaly

Susan Samson, MD, PhD, of Baylor College of…

Jun 16, 2020| Posted in: Cancers, Endocrine Disorders, Metabolic Disorders

Acromegaly

Acromegaly is a rare endocrine disorder due to…

May 8, 2020| Posted in: Congenital And Genetic Conditions, Endocrine Disorders, Neurology/Nervous System Diseases, News, Ophthalmology/Eye Diseases, Regulations, Treatment

Positive Phase 2 Data With GABA-A Agonist to Treat Fragile X Syndrome

Ovid Pharmaceutics has announced their novel delta (δ)-selective…

May 5, 2020| Posted in: Diagnosis, Drug Development, Endocrine Disorders, News, Regulations, Treatment

FDA Approves New Leuprolide Acetate Formulation to Treat Central Precocious Puberty

The US Food and Drug Administration (FDA) has…

May 4, 2020| Posted in: Congenital And Genetic Conditions, Endocrine Disorders, Heart Diseases, Kidney And Urinary Diseases, Ophthalmology/Eye Diseases

CHARGE Syndrome

CHARGE syndrome is a complex genetic condition, which…

Rare Disease Clinical Trials CME Program

Learn about clinical trials and rare diseases through these brief courses that are certified for CME and CNE credit.

Heather Lau, MD, MS, NYU School of Medicine, New York, NY
Morie A Gertz, MD, Mayo Clinic, Rochester, MN
Timothy Craig, DO, Penn State University, Hershey, PA
Eric T. Wong, MD, Harvard Medical School, Boston, MA

CME Program: Fabry Disease Highlights from WORLDSymposium 2020

Ozlem Goker-Alpan, MD highlights the latest Fabry disease information from the WORLDSymposium and provides expert analysis of its clinical relevance for members of the care team in order to help them care for patients with this rare disease.

WHIM Syndrome Learning Center

WHIM syndrome is a rare, congenital primary immunodeficiency disorder associated with severe neutropenia that affects all ages. However, due to the heterogeneous presentation of the disease, coupled with lack of awareness of the condition, the diagnosis may be delayed, sometimes even into adulthood.

Endocrine Disorders

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