Kidney And Urinary Diseases
Jan 8, 2021| Posted in: Congenital And Genetic Conditions, Heart Diseases, Hematologic Disorders, Kidney And Urinary Diseases, Lysosomal Storage Disorders, Metabolic Disorders, Neurology/Nervous System Diseases, Ophthalmology/Eye Diseases, Skin Conditions
Overview of Fabry Disease
Robert Hopkin, MD, Associate Professor of Clinical Pediatrics… Jan 4, 2021| Posted in: Autoimmune / Autoinflammatory Disorders, Cancers, Congenital And Genetic Conditions, Drug Development, Endocrine Disorders, Gastrointestinal Diseases, Heart Diseases, Hematologic Disorders, Kidney And Urinary Diseases, Lung Diseases, Lysosomal Storage Disorders, Metabolic Disorders, Musculoskeletal Diseases, Neurology/Nervous System Diseases, News, Ophthalmology/Eye Diseases, Skin Conditions, Treatment
Orphan Drugs Currently Under Review by the FDA
Every potential Food and Drug Administration (FDA) approval… Nov 23, 2020| Posted in: Congenital And Genetic Conditions, Kidney And Urinary Diseases, Metabolic Disorders
FDA Approves Lumasiran to Treat Primary Hyperoxaluria Type 1
Pritesh J. Gandhi, PharmD of Alnylam Pharmaceuticals provides an… Nov 23, 2020| Posted in: Congenital And Genetic Conditions, Kidney And Urinary Diseases, Metabolic Disorders
Alnylam, and the PH1 Community, Waiting for the FDA to Approve Lumasiran
Pritesh J. Gandhi, PharmD of Alnylam Pharmaceuticals discusses the… Nov 10, 2020| Posted in: Autoimmune / Autoinflammatory Disorders, Drug Development, Kidney And Urinary Diseases
Clinical Trials for Lupus Nephritis
Richard A. Furie, MD, from Northwell Health explains… Nov 2, 2020| Posted in: Cancers, Congenital And Genetic Conditions, Endocrine Disorders, Kidney And Urinary Diseases, Neurology/Nervous System Diseases, Ophthalmology/Eye Diseases, Treatment
MK-6482 to Treat Renal Cell Carcinoma in Von Hippel-Lindau Disease Patients
Eric Jonasch, MD, Professor, Department of Genitourinary Medical… Oct 27, 2020| Posted in: Cancers, Congenital And Genetic Conditions, Endocrine Disorders, Hematologic Disorders, Kidney And Urinary Diseases, Neurology/Nervous System Diseases, Ophthalmology/Eye Diseases
What is Von Hippel-Lindau Disease?
Eric Jonasch, MD, Professor, Department of Genitourinary Medical… Oct 15, 2020| Posted in: Congenital And Genetic Conditions, Endocrine Disorders, Expert Perspectives, Kidney And Urinary Diseases, Musculoskeletal Diseases, Treatment
Approval of Burosumab-twza for Treating Tumor-Induced Osteomalacia
Erik Harris, Executive Vice President and Chief Commercial… Oct 2, 2020| Posted in: Advocacy, Autoimmune / Autoinflammatory Disorders, Cancers, Congenital And Genetic Conditions, Diagnosis, Drug Development, Endocrine Disorders, Featured, Gastrointestinal Diseases, Heart Diseases, Hematologic Disorders, Kidney And Urinary Diseases, Lung Diseases, Lysosomal Storage Disorders, Metabolic Disorders, Musculoskeletal Diseases, Neurology/Nervous System Diseases, News, Ophthalmology/Eye Diseases, Regulations, Skin Conditions, Treatment
A Preview of NORD’s Rare Summit 2020
Peter Saltonstall, President and Chief Executive Officer of… Sep 4, 2020| Posted in: Congenital And Genetic Conditions, Drug Development, Kidney And Urinary Diseases, Metabolic Disorders, Treatment