• Diseases
  • Featured
  • CME / CE
  • Podcasts
  • Resources
    • Orphan Drug Approvals
    • Priority Review Voucher
    • Rare Disease Recognition and Awareness Days
  • About Us
  • Diseases
  • Featured
  • CME / CE
  • Podcasts
  • Resources
    • Priority Review Voucher Tracking
    • Rare Disease Recognition and Awareness Days
    • 2026 Orphan Drugs: PDUFA Dates and FDA Approvals
  • About Us
  • Sign Up for our Newsletter
  • Spotlight
  • Spinal Muscular Atrophy
  • Narcolepsy
  • Prader-Willi Syndrome
Newsletter
Newsletter

Treatment With Xywav (Low Sodium Oxybate) in Patients With Narcolepsy and Idiopathic Hypersomnia

by Madaline Spencer | Jul 6, 2026

Logan Schneider, MD, Adjunct Clinical Associate Professor of Psychiatry and Behavioral Sciences at Stanford University, discusses treatment with Xywav (low sodium oxybate) in patients with sleep disorders, narcolepsy and idiopathic hypersomnia.    ...

FDA Approves Lumvoa (Veligrotug) for Thyroid Eye Disease

by Madaline Spencer | Jul 3, 2026

The US Food and Drug Administration (FDA) has approved Lumvoa (veligrotug) for the treatment of thyroid eye disease (TED), regardless of TED’s duration or activity. TED is a chronic endocrine, autoimmune disease characterized by immune-mediated orbital...

Are All Cancers Rare Cancers? The Need for Better Classification Systems

by Madaline Spencer | Jul 2, 2026

Chadi Nabhan, MD, Hematologist and Oncologist, Chief Medical Officer at Ryght AI, and Vivek Subbiah, MD, Professor of Medicine at Stanford University and Executive Medical Director of Novel Therapies & Clinical Trial Network at Stanford Health Care, discuss the...

The Role of Rusfertide in Decreasing Phlebotomies in Patients With Polycythemia Vera

by Madaline Spencer | Jul 1, 2026

Andrew Kuykendall, MD, Clinical Researcher at Moffitt Cancer Center, discusses the role of rusfertide in decreasing phlebotomies in patients with polycythemia vera (PV).     PV is a condition characterized by an increased number of red blood cells. Affected...

FDA Grants Full Approval to Afami-Cel for Patients With Synovial Sarcoma

by Madaline Spencer | Jun 30, 2026

The US Food and Drug Administration (FDA) has granted full approval to Tecelra (afamitresgene autoleucel; afami-cel) and expanded its indication to include patients ages 12 years and older with unresectable or metastatic synovial sarcoma whose disease has progressed...
Page 2 of 131«12345...102030...»Last »
 Categories
  • Autoimmune / Autoinflammatory Disorders
  • Cancers
  • Congenital And Genetic Conditions
  • Endocrine Disorders
  • Gastrointestinal Diseases
  • Heart Diseases
  • Hematologic Disorders
  • Kidney And Urinary Diseases
  • Lung Diseases
  • Lysosomal Storage Disorders
  • Metabolic Disorders
  • Musculoskeletal Diseases
  • Neurology/Nervous System Diseases
  • Ophthalmology/Eye Diseases
  • Skin Conditions
d Topics
  • Advocacy
  • Diagnosis
  • Drug Development
  • Regulations
  • Treatment
 Contact

Advertising / Promoted Programs
[email protected]

CE / Continuing Education
[email protected]
  • Follow
  • Follow
  • Follow
  • Follow
  • Follow
  • Login
Copyright © 2026 CheckRare. All Rights Reserved.
  • Terms and Conditions
  • Privacy
  • Do Not Use My Personal Information
  • Login
  • Sign Up
Forgot Password?
Lost your password? Please enter your username or email address. You will receive a link to create a new password via email.
body::-webkit-scrollbar { width: 7px; } body::-webkit-scrollbar-track { border-radius: 10px; background: #f0f0f0; } body::-webkit-scrollbar-thumb { border-radius: 50px; background: #dfdbdb }
We use cookies on our website to give you the most relevant experience by remembering your preferences and repeat visits. By clicking “Accept”, you consent to the use of ALL the cookies.
Do not sell my personal information.
Cookie Settings Accept
Manage consent

Privacy Overview

This website uses cookies to improve your experience while you navigate through the website. Out of these, the cookies that are categorized as necessary are stored on your browser as they are essential for the working of basic functionalities of the website. We also use third-party cookies that help us analyze and understand how you use this website. These cookies will be stored in your browser only with your consent. You also have the option to opt-out of these cookies. But opting out of some of these cookies may affect your browsing experience.
Necessary
Always Enabled
Necessary cookies are absolutely essential for the website to function properly. These cookies ensure basic functionalities and security features of the website, anonymously.
CookieDurationDescription
cookielawinfo-checkbox-analytics11 monthsThis cookie is set by GDPR Cookie Consent plugin. The cookie is used to store the user consent for the cookies in the category "Analytics".
cookielawinfo-checkbox-functional11 monthsThe cookie is set by GDPR cookie consent to record the user consent for the cookies in the category "Functional".
cookielawinfo-checkbox-necessary11 monthsThis cookie is set by GDPR Cookie Consent plugin. The cookies is used to store the user consent for the cookies in the category "Necessary".
cookielawinfo-checkbox-others11 monthsThis cookie is set by GDPR Cookie Consent plugin. The cookie is used to store the user consent for the cookies in the category "Other.
cookielawinfo-checkbox-performance11 monthsThis cookie is set by GDPR Cookie Consent plugin. The cookie is used to store the user consent for the cookies in the category "Performance".
viewed_cookie_policy11 monthsThe cookie is set by the GDPR Cookie Consent plugin and is used to store whether or not user has consented to the use of cookies. It does not store any personal data.
Functional
Functional cookies help to perform certain functionalities like sharing the content of the website on social media platforms, collect feedbacks, and other third-party features.
Performance
Performance cookies are used to understand and analyze the key performance indexes of the website which helps in delivering a better user experience for the visitors.
Analytics
Analytical cookies are used to understand how visitors interact with the website. These cookies help provide information on metrics the number of visitors, bounce rate, traffic source, etc.
Advertisement
Advertisement cookies are used to provide visitors with relevant ads and marketing campaigns. These cookies track visitors across websites and collect information to provide customized ads.
Others
Other uncategorized cookies are those that are being analyzed and have not been classified into a category as yet.
Save & Accept