by Madaline Spencer | Jan 26, 2026
Guy Young, MD, Children’s Hospital Los Angeles, discusses the SWITCH clinical trial design for patients with hemophilia A. Hemophilia A is an inherited bleeding disorder in which the blood does not clot normally. People with hemophilia A will bleed more than...
by Madaline Spencer | Jan 23, 2026
Christine Gustafson, Executive Director and CEO of the TED Community Organization, discusses her personal journey with thyroid eye disease (TED) and why she started the TED Community Organization. TED is a chronic endocrine, autoimmune disease characterized...
by Madaline Spencer | Jan 22, 2026
Recently, results from a phase 2a study evaluating SGX945 (dusquetide) for the treatment of Behçet’s disease were published in Rheumatology (Oxford). Behçet’s disease is a rare vasculitis characterized by inflammation and swelling of blood vessels. It often affects...
by Madaline Spencer | Jan 21, 2026
Janet Legare, MD, Professor of Pediatrics in the Division of Genetics at the University of Wisconsin, discusses week 52 results of TransCon CNP (navepegritide) in children with achondroplasia. Achondroplasia is a genetic disorder that prevents the...
by Madaline Spencer | Jan 20, 2026
Catherine M. Broome, MD, Professor of Medicine and Director of Cellular Apheresis, Lombardi Cancer Center, MedStar Georgetown University, discusses real world safety data of Enjaymo (sutimlimab) in patients with cold agglutinin disease (CAD). CAD is a rare type...
