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Treatment With Elritercept for Patients With Myelofibrosis

by Madaline Spencer | Jan 7, 2026

Ciro Rinaldi, MD, Consultant Hematologist and Professor of Hematology at United Lincolnshire Hospital, discusses treatment with elritercept for patients with myelofibrosis (MF).     MF is characterized by the buildup of scar tissue in the bone marrow. The...

Duchenne Muscular Dystrophy (DMD) and Metachromatic Leukodystrophy (MLD) Recommended Uniform Screening Panel

by Madaline Spencer | Jan 6, 2026

The U.S. Department of Health and Human Services (HHS) has approved the addition of Duchenne muscular dystrophy (DMD) and metachromatic leukodystrophy (MLD) to the Recommended Uniform Screening Panel (RUSP). DMD and MLD DMD is a rare genetic, neuromuscular condition...

Updated Phase 2 Results of Telquetamab + Teclistamab in Multiple Myeloma

by Madaline Spencer | Jan 6, 2026

Saad Usmani, MD, Myeloma Specialist and Cellular Therapist at Memorial Sloan Kettering Cancer Center, discusses updated results from the phase 2 RedirecTT-1 study of telquetamab + teclistamab in patients with multiple myeloma (MM).     MM is a form of cancer...

FDA Approves Obstructive Hypertrophic Cardiomyopathy Treatment

by Madaline Spencer | Jan 5, 2026

The U.S. Food and Drug Administration (FDA) has approved Myqorzo (aficamten) for the treatment of adults with symptomatic obstructive hypertrophic cardiomyopathy (oHCM). oHCM is a rare genetic heart condition characterized by excessive growth of heart muscle cells....

Results from the CARTITUDE-4 Clinical Trial in Multiple Myeloma

by Madaline Spencer | Jan 5, 2026

Binod Dhakal, MD, Associate Professor of Medicine at Medical College of Wisconsin, discusses results from the CARTITUDE-4 clinical trial in patients with multiple myeloma (MM).     MM is a form of cancer that occurs due to abnormal and uncontrolled growth of...
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