by Madaline Spencer | Jan 12, 2026
A recent post hoc analysis of long-term efficacy of migalastat in females with Fabry disease was published in the Journal of Medical Genetics. Fabry disease is a rare lysosomal storage disease characterized by a deficiency of the enzyme alpha-galactosidase...
by Madaline Spencer | Jan 9, 2026
The U.S. Food and Drug Administration (FDA) has approved Cablivi (caplacizumab) for the treatment of pediatric patients ages 12 years and older with acquired thrombotic thrombocytopenic purpura (aTTP) in combination with plasma exchange and immunosuppressive therapy. ...
by Madaline Spencer | Jan 9, 2026
Vicki Salemi, Career Expert, discusses current trends in the healthcare job market and expectations for 2026. Recent data from the 2025 Monster Healthcare Market Report shows how the healthcare industry is changing. Through an analysis of healthcare job...
by Madaline Spencer | Jan 8, 2026
Jun Ho Jang, MD, PhD, Professor, Division of Hematology-Oncology at Samsung Medical Center, discusses results from an open-label extension study testing pozelimab plus cemdisiran combination therapy in patients with paroxysmal nocturnal hemoglobinuria (PNH), who...
by Madaline Spencer | Jan 7, 2026
The U.S. Food and Drug Administration (FDA) has approved Aqvesme (mitapivat) for the treatment of anemia in adults with alpha- or beta-thalassemia. Alpha- and beta-thalassemia are blood disorders that reduce the body’s production of hemoglobin. Affected people...