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How the TED Community Organization Helps Patients With Thyroid Eye Disease Take Their Lives Back

by Madaline Spencer | Jan 23, 2026

Christine Gustafson, Executive Director and CEO of the TED Community Organization, discusses her personal journey with thyroid eye disease (TED) and why she started the TED Community Organization.     TED is a chronic endocrine, autoimmune disease characterized...

Phase 2 Results of Dusquetide in the Treatment of Oral Ulcers Caused by Behçet’s Disease

by Madaline Spencer | Jan 22, 2026

Recently, results from a phase 2a study evaluating SGX945 (dusquetide) for the treatment of Behçet’s disease were published in Rheumatology (Oxford). Behçet’s disease is a rare vasculitis characterized by inflammation and swelling of blood vessels. It often affects...

Week 52 Results of TransCon CNP (Navepegritide) in Children With Achondroplasia

by Madaline Spencer | Jan 21, 2026

Janet Legare, MD, Professor of Pediatrics in the Division of Genetics at the University of Wisconsin, discusses week 52 results of TransCon CNP (navepegritide) in children with achondroplasia.     Achondroplasia is a genetic disorder that prevents the...

Real World Safety Data of Enjaymo (Sutimlimab) in Patients With Cold Agglutinin Disease

by Madaline Spencer | Jan 20, 2026

Catherine M. Broome, MD, Professor of Medicine and Director of Cellular Apheresis, Lombardi Cancer Center, MedStar Georgetown University, discusses real world safety data of Enjaymo (sutimlimab) in patients with cold agglutinin disease (CAD).   CAD is a rare type...

Long-term Efficacy of Rilzabrutinib in Patients With Immune Thrombocytopenia

by Madaline Spencer | Jan 19, 2026

David Kuter, MD, DPhil, Professor of Medicine at Harvard Medical School, Massachusetts General Hospital, discusses treatment with rilzabrutinib in patients with immune thrombocytopenia (ITP).    ITP is an autoimmune bleeding disorder characterized by too few...
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