by Madaline Spencer | Dec 30, 2024
James Squires, MD, University of Pittsburgh, discusses recent data regarding Bylvay (odevixibat) in patients with progressive familial intrahepatic cholestasis (PFIC) and Alagille syndrome. PFIC is a heterogeneous group of autosomal recessive disorders of...
by Madaline Spencer | Dec 27, 2024
Peter Richardson, MD, Executive Vice President and Chief Scientific Officer of Mallinckrodt Pharmaceuticals, discusses recent data regarding Terlivaz (terlipressin) for hepatorenal syndrome (HRS). HRS is a form of renal failure that occurs in patients...
by Madaline Spencer | Dec 23, 2024
Alan Krasner, MD, Chief Medical Officer of Crinetics Pharmaceuticals, discusses the new drug application (NDA) submission of paltusotine for treating acromegaly. Acromegaly is a rare hormonal disorder resulting from the overproduction of growth hormone in the...
by Madaline Spencer | Dec 20, 2024
Carol Roberts, President, The PBCers Organization, discusses the symptom burden of primary biliary cholangitis (PBC). PBC is a chronic, progressive, autoimmune, liver disease in which the bile ducts become inflamed and damaged. This leads to the buildup...
by Madaline Spencer | Dec 19, 2024
Tanita Allen, a patient advocate with Huntington disease, discusses her diagnostic journey and advocacy work. Huntington’s disease is an inherited condition that causes progressive degeneration of central neurons. It is caused by changes in the HTT gene...
