by Madaline Spencer | Mar 5, 2025
Daniel Lewi, Founder of the CATS Foundation, and Kathleen Flynn, CEO of the National Tay-Sachs & Allied Diseases Association (NTSAD), discuss an industry-advocacy collaboration to optimize clinical trial design through a patient-centric approach. An...
by Madaline Spencer | Feb 28, 2025
February 28 Is Rare Disease Day! Rare Disease Day, observed on the last day of February every year, is a reminder of the challenges faced by those living with a rare disease. Established in 2008 by EURORDIS (The European Organisation for Rare Diseases), the day serves...
by Madaline Spencer | Feb 24, 2025
Alix Arnaud, Director of Health Economic and Value Assessment BP at Sanofi, discusses the cost of efanesoctocog alfa compared with other Factor VIII replacement therapies for major surgeries in patients with hemophilia A. Hemophilia A is an inherited...
by Madaline Spencer | Feb 16, 2025
Gus Baker, PhD, International Bureau for Epilepsy, discusses a social media listening study looking at the experiences of women of childbearing age with epilepsy. A social media listening study was conducted to identify key topics of conversation, unmet...
by Madaline Spencer | Feb 15, 2025
Danya Kaye, UCB Pharma, discusses a study observing the profound burden of prolonged seizures in patients with epilepsy. The objective of this study was to explore the experiences of people with epilepsy living with prolonged seizures and their...
