Education Campaign for Thyroid Eye Disease

by | Sep 3, 2025

Margarita Ochoa-Maya, MD, Medical Director of the Rare Disease Business Unit at Amgen, discusses the TEDucation campaign for thyroid eye disease (TED).   TED is a rare autoimmune disease that can dramatically impact a person’s vision. The condition often occurs...

Mental Health in Patients With Acromegaly

by | Sep 1, 2025

Lori Bulpett, Manager of Patient Advocacy at Chiesi Global Rare Diseases, discusses mental health in patients with acromegaly.     Acromegaly is a hormonal disorder that results from the overproduction of growth hormone in the pituitary gland. It is most...

SMAshing My Limits

by | Aug 29, 2025

Tracey Dawson, PhD, SVP, U.S. Therapeutic Area Head of Neuroscience at Novartis, discusses the SMAshing My Limits campaign.     Spinal muscular atrophy (SMA) is a group of genetic neuromuscular disorders that affect the motor neurons. The loss of motor...

Recordati Rare Disease Initiatives

by | Aug 25, 2025

Mohamed Ladha, President and General Manager for Recordati Rare Diseases North America, discusses the company’s rare disease initiatives.     The U.S. branch of Recordati was established in 2013 with a focus on products to treat patients with rare inherited...