by Peter Ciszewski | Feb 8, 2021
Ron Cooper, President and CEO of Albireo Pharma, discusses the effect the Orphan Drug Act has had on rare disease pharmaceutical companies. As Mr. Cooper explains, the Orphan Drug Act of 1983, which facilitated the development of orphan drugs in the United...
by James Radke | Feb 5, 2021
Maurice Ohayon, MD, PhD, Professor of Psychiatry and Behavioral Sciences from Stanford University, provides a brief overview of narcolepsy. Narcolepsy is a rare disorder characterized by excessive sleepiness during the day, often with periods of brief...
by Peter Ciszewski | Feb 5, 2021
Auris Huen, MD, PharmD, Assistant Professor, MD Anderson Cancer Center, Department of Dermatology provides an overview of Sézary Syndrome, a subtype of Cutaneous T-cell lymphoma (CTCL). Cutaneous T-cell lymphoma belongs to the non-Hodgkin lymphoma class of...
by James Radke | Feb 4, 2021
Barbara Burton, MD, of Northwestern University Feinberg School of Medicine, provides an overview of the various mucopolysaccharidosis (MPS) conditions. The MPSs are a group of lysosomal storage disorders that include MPS I (e.g., Hurler syndrome), MPS II...
by Peter Ciszewski | Feb 4, 2021
Auris Huen, MD, PharmD, Assistant Professor, MD Anderson Cancer Center, Department of Dermatology provides an overview of Mycosis Fungoides, a subtype of cutaneous T-cell lymphoma (CTCL). Cutaneous T-cell lymphoma belongs to the non-Hodgkin lymphoma class of...
