by James Radke | Jan 5, 2023
Mechanism of Action of SRP-9001, A Gene Therapy For Duchenne Muscular Dystrophy Lisa Borland, Vice President of Global Medical Affairs at Sarepta Therapeutics, discusses the mechanism of action of SRP-9001, an investigational gene transfer therapy for...
by James Radke | Feb 14, 2022
Jonathan Wall, PhD, Director of the University of Tennessee Graduate School of Medicine’s Amyloidosis and Cancer Theranostics Program and Co-founder & Interim Chief Scientific Officer at Attralus, discusses data from a phase 1/2 trial evaluating the ability...
by James Radke | Oct 29, 2021
Sima Rozati, MD, Assistant Professor of Dermatology at the Johns Hopkins University School of Medicine, gives an overview of cutaneous T-cell lymphoma (CTCL). CTCL belongs to the non-Hodgkin lymphoma family as a rare group of malignancies. CTCL involves...
by James Radke | Oct 8, 2021
James Underberg, MD, Clinical Assistant Professor of Medicine at NYU Medical School, provides an overview of homozygous familial hypercholesterolemia (HoFH). HoFH is a genetic disorder that results in severe impairment of the low-density lipoprotein receptor...
by James Radke | Jul 20, 2021
Daniel Auclair, MD, Chief Scientific Officer of the Multiple Myeloma Research Foundation (MMRF), discusses a lesser known disparity in multiple myeloma patients – their location. Multiple myeloma is a rare blood cancer associated with uncontrolled growth of...
