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Efficacy of Atrasentan To Treat Patients With IgA Nephropathy

by Madaline Spencer | Apr 18, 2025

Richard Lafayette, MD, Professor of Medicine, Nephrology and Director of the Glomerular Disease Center at Stanford University Medical Center, discusses the recent approval of Vanrafia (atrasentan) for patients with IgA nephropathy (IgAN).     IgAN is a rare...

New FDA-Approved C3 Glomerulopathy (C3G) Treatment Targets Underlying Cause of Disease

by Madaline Spencer | Apr 16, 2025

Carla Nester, MD, Professor of Pediatrics-Nephrology at the University of Iowa, discusses the recent U.S. Food and Drug Administration (FDA) approval of iptacopan as the first and only treatment of adults with C3 glomerulopathy (C3G).     C3G is a rare...

FORWARD-53 Clinical Trial in Duchenne Muscular Dystrophy Shows Promise

by Madaline Spencer | Apr 14, 2025

Paul Bolno, MD, President and Chief Executive Officer of Wave Life Sciences, discusses positive results from the FORWARD-53 clinical trial evaluating WVE-N531 in patients with Duchenne muscular dystrophy (DMD) amenable to exon 53 skipping.     DMD affects...

First Treatment (Diazoxide Choline) Approved for Hyperphagia in Prader-Willi Syndrome

by Madaline Spencer | Apr 8, 2025

Ashley Shoemaker, MD, Associate Professor of Pediatrics and Pediatric Endocrinology at Vanderbilt University, discusses the approval of Vykat XR (diazoxide choline) for the treatment of hyperphagia in patients ages 4 years and older with Prader-Willi syndrome (PWS)....

Results From the Phase 1/2 EXPLORE44 Clinical Trial for Duchenne Muscular Dystrophy

by Madaline Spencer | Apr 2, 2025

Aravindhan Veerapandiyan, MD, Assistant Professor of Pediatrics, University of Arkansas and Arkansas Children’s Hospital, discusses results from the phase 1/2 EXPLORE44 clinical trial for Duchenne muscular dystrophy (DMD).     DMD affects the muscles,...
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