Genetic Modifiers for Treatment in Lysosomal Disorders

Andrés Klein, PhD, Associate Professor and Director of the Doctorate Program in Sciences and Innovation in Medicine at Universidad del Desarrollo, Santiago, Chile, discusses the identification of genetic modifiers for treatment in lysosomal disorders.    ...

Gaucher Community Alliance

Madelyn Schloss, Social Media and Development Associate for Gaucher Community Alliance, discusses the organization.     The Gaucher Community Alliance is a non-profit organization run by patients with Gaucher disease, offering advocacy, education, patient...