Applied Therapeutics Overview

Shoshana Shendelman, PhD, President and Chief Executive Officer of Applied Therapeutics provides a brief overview of the orphan drug company.     As Dr Shendelman explains, Applied Therapeutics is a biopharmaceutical company developing a pipeline of novel...

Overview of Homozygous Familial Hypercholesterolemia

Mary P. McGowan, MD, chief medical officer of the Family Heart Foundation provides an overview of homozygous familial hypercholesterolemia (HoFH).     HoFH is a rare genetic disorder that results in severe impairment of the low-density lipoprotein receptor...

IgA Nephropathy Explained

Richard Lafayette, MD, FACP, Director of the Stanford Glomerular Disease Center, and Rheumatologist at Stanford Health Care, describes the current standard of care for immunoglobulin A (IgA) nephropathy.      IgA nephropathy (Berger’s disease) is a rare...

Multiple Myeloma Trial Results

Binod Dhakal, MD, Associate Professor at Medical College of Wisconsin discusses results of the phase 3 multiple myeloma clincial trial. This trial compared Ciltacabtagene autoleucel to standard of care in patients with lenalidomide-refractory multiple myeloma.  ...

Oral Octreotide Acromegaly Treatment

Patrick Lewis, PharmD, Senior Director, Medical Affairs at Amryt Pharma discusses the latest data presented at ENDO 2023 on oral octreotide to treat acromegaly.     Acromegaly is a rare endocrine disorder due to excess levels of growth hormone (GH). A benign...