by Madaline Spencer | Sep 1, 2025
Lori Bulpett, Manager of Patient Advocacy at Chiesi Global Rare Diseases, discusses mental health in patients with acromegaly. Acromegaly is a hormonal disorder that results from the overproduction of growth hormone in the pituitary gland. It is most...
by Madaline Spencer | Aug 29, 2025
The U.S. Food and Drug Administration (FDA) has approved Papzimeos (zopapogene imadenovec-drba) for the treatment of adults with recurrent respiratory papillomatosis (RRP). RRP is a rare viral disease characterized by benign tumors in the respiratory tract. The tumors...
by Madaline Spencer | Aug 29, 2025
Tracey Dawson, PhD, SVP, U.S. Therapeutic Area Head of Neuroscience at Novartis, discusses the SMAshing My Limits campaign. Spinal muscular atrophy (SMA) is a group of genetic neuromuscular disorders that affect the motor neurons. The loss of motor...
by Madaline Spencer | Aug 28, 2025
Mario Maldonado, MD, Global Head of Clinical Development for Endocrinology at Recordati Rare Diseases, discusses Recordati’s presentations at ENDO 2025. LINC6 Clinical Trial LINC 6 is an ongoing, prospective observational study evaluating the long-term...
by Madaline Spencer | Aug 27, 2025
Alan Krasner, MD, Chief Endocrinologist at Crinetics Pharmaceuticals, discusses atumelnant for the treatment of patients with congenital adrenal hyperplasia (CAH). CAH is a genetic condition characterized by an enzyme deficiency in the adrenal glands....
