by Madaline Spencer | May 6, 2026
The US Food and Drug Administration (FDA) has approved Jakafi XR (ruxolitinib) extended-release tablets for the treatment of three rare hematologic conditions. The indications include the treatment of: (1) adults with intermediate- or high-risk myelofibrosis (MF); (2)...
by Madaline Spencer | May 5, 2026
Dena Sherwood, mother to a neuroblastoma survivor and Founder of Arms Wide Open Childhood Cancer Foundation, discusses CureFest 2026. Ms. Sherwood and her family founded the Arms Wide Open Childhood Cancer Foundation following the struggles their son...
by Madaline Spencer | May 4, 2026
Tuan Vu, MD, Professor, Department of Neurology at the University of South Florida, discusses positive results of cemdisiran in patients with generalized myasthenia gravis (gMG). MG is a chronic autoimmune neuromuscular disease characterized by weakness...
by Madaline Spencer | May 1, 2026
A study published in the Annals of the American Thoracic Society analyzed results from the ELEVATE-1 clinical trial testing the effects of rodatristat ethyl on daily activity in patients with pulmonary arterial hypertension (PAH). PAH is a rare condition affecting the...
by Madaline Spencer | Apr 30, 2026
Dareen D. Siri, MD, FAAAAI, FACAAI is a board-certified allergist and immunologist practicing at Midwest Allergy Sinus Asthma, based in central Illinois. She talked with CheckRare about a unique, rare disorder called systemic mastocytosis. Systemic...
