Rare Disease Recognition and Awareness Days

by | Jun 6, 2025

Rare disease awareness days serve an important purpose of informing the public, creating community, and raising money to support funding towards new research and treatments. Below is a calander containing rare disease awareness days and months as well as more...

Generalized Myasthenia Gravis

by | Jan 17, 2024

  Cynthia Qi, Health Economics Outcomes Researcher at Argenx discusses her poster presentation focused on generalized myasthenia gravis.     Transcription: The poster I have is about the real-world outcomes of myasthenia gravis patients receiving...

Baylor Genetics Data at NORD, NSGC, and ASHG

by | Jan 16, 2024

Christine Eng, Chief Medical Officer at Baylor Genetics, discusses the information her company presented at various conferences.     Transcription: We are presenting at these three conferences. NORD is really a unique conference because it brings together...

Myasthenia Gravis and Real-Life Data

by | Jan 15, 2024

  Cynthia Qi, Health Economics Outcomes Researcher at Argenx, discusses myasthenia gravis and real-life data.     Transcription: Hello, everyone. My name is Cynthia Qi. I am a Health Economics Outcomes Researcher at Argenx. I’ve been working in...

Myasthenia Gravis Treatment Options

by | Jan 12, 2024

Kimberly Moran, PhD, MBA, Head of US Rare Diseases at UCB, discuses new treatment options for myasthenia gravis, Transcription: One, we don’t make the clinical decisions. That’s what healthcare practitioners do. Most of their job is to really understand...