by Madaline Spencer | Jul 21, 2025
Amélie Lothe, PhD, Head of Global Medical Community of Rare Epilepsies at UCB, discusses positive data on fenfluramine for the treatment of CDKL5 deficiency disorder (CDD). CDD is a rare, genetic developmental and epileptic encephalopathy (DEE)...
by Madaline Spencer | Jul 18, 2025
Sandra Silvestri, MD, PhD, Chief Medical Officer at Ipsen, discusses the effect of elafibranor on fatigue in patients with primary biliary cholangitis (PBC). PBC is a chronic, progressive, autoimmune, liver disease in which the bile ducts become inflamed...
by Madaline Spencer | Jul 17, 2025
Ann Leon, PharmD, Global Medical Affairs Leader of Benign Hematology at Johnson & Johnson, discusses the unmet needs of patients with warm autoimmune hemolytic anemia (wAIHA). wAIHA is a rare hematologic condition characterized by the immune system...
by Madaline Spencer | Jul 16, 2025
Erin Dunbar, MD, founding physician of the Brain Tumor Center and Director of Neuro-Oncology at Piedmont Atlanta Hospital, discusses the current landscape of glioblastoma. Glioblastoma is a malignant brain tumor that develops from an astrocyte brain...
by Madaline Spencer | Jul 15, 2025
Takeda has announced positive data from two phase 3 clinical trials of oveporexton in patients with narcolepsy type 1 (NT1). NT1 is a rare, chronic neurological disorder characterized by excessive daytime sleepiness (EDS) and cataplexy. It is caused by reduced levels...
