by Peter Ciszewski | Dec 9, 2020
Lisa Nachtigall, MD, Clinical Director, Neuroendocrine and Pituitary Clinical Center at Massachusetts General Hospital, and Associate Professor at Harvard Medical School, discusses some of the challenges of diagnosing Acromegaly. Acromegaly is a rare endocrine...
by Peter Ciszewski | Dec 8, 2020
Ron Cooper, President and CEO of Albireo Pharma discusses the results from two clinical trials assessing odevixibat to treat progressive familial intrahepatic cholestasis (PFIC). PFIC is a rare genetic disorder that causes progressive, life-threatening liver...
by Peter Ciszewski | Dec 7, 2020
Kristin Highland, MD of the Cleveland Clinic discusses the results for the ongoing SENSCIS-ON trial testing nintedanib to treat interstitial lung disease in patients with systemic sclerosis. Systemic sclerosis is a rare autoimmune disease that is associated...
by Peter Ciszewski | Dec 4, 2020
The U.S. Food and Drug Administration (FDA) has approved Orladeyo (berotralstat), a once-daily, pill as a prophylaxis treatment for hereditary angioedema (HAE) attacks. More specifically, the drug is indicated to treat adults and pediatric patients 12 years and older...
by Peter Ciszewski | Dec 4, 2020
Fariba Navid, MD, Associate Professor of Clinical Pediatrics, Keck School of Medicine of USC, announces her involvement in a trial for nirogacestat as a treatment for Desmoid tumors in pediatric patients. Desmoid tumors are benign tumors that can grow anywhere...
