Dup15q Syndrome Research

  Vanessa Vogel-Farley, Executive Director, Dup15q Alliance discusses her Alliance and some of the research for Dup15q syndrome, the common name for chromosome 15q11.2-q13.1 duplication syndrome. Dup15q syndrome is the common name for chromosome 15q11.2-q13.1...

Rare Disease Drug Development at Albireo

  Ron Cooper, President and CEO of Albireo, discusses drug development at Albireo, which has a clinical trial in progressive familial intrahepatic cholestasis (PFIC), a rare genetic condition that affects the liver. PFIC is estimated to affect between one in...

Positive Results in Phase 3 Cushing’s Syndrome Trial

Strongbridge Biopharma’s pivotal phase 3 SONICS study evaluating levoketoconazole (Recorlev) for the treatment of endogenous Cushing’s syndrome achieved statistical significance of its pre-specified primary endpoint. According to the company, 30% of patients...

Alnylam Overview

  Editor’s Note: This interview was conducted at #BIO2018. Please pardon the background noise. Barry Greene, President of Alnylam, joined the company in 2003 and has more than 25 years of experience in healthcare, pharmaceutical, and biotechnology...

Interecept Pharma: Focused on Non-Viral Liver Diseases

  Gail Cawkwell, MD, PhD, Senior Vice President, Medical Affairs at Intercept, provides an overview of the company. Intercept is a biopharmaceutical company focused on the development and commercialization of novel therapeutics to treat progressive non-viral...