by Peter Ciszewski | Nov 23, 2017
Len Walt, Vice President, Head of Medical Affairs, Sobi in North America, provides an overview of Still’s disease, a rare inflammatory disorder that affects the entire body, and how these patients typically present to their physicians. Still’s disease is...
by Peter Ciszewski | Nov 20, 2017
PellePharm, a clinical-stage biopharmaceutical company focusing on rare genetic dermatological conditions, announced that the Food and Drug Administration (FDA) has granted both Breakthrough Therapy Designation and Orphan Drug Designation to topical patidegib for...
by Peter Ciszewski | Nov 20, 2017
Jessica Fein’s daughter Dalia has the mitochondrial disease MERRF Syndrome. Jessica spoke with us at the Rare Disease Film Festival, an event showcasing a myriad of films from around the world that addresses the challenges of life with a rare disease. Myoclonic...
by Peter Ciszewski | Nov 19, 2017
Philippe Maitre, Executive Vice President, US Operations for Onxeo discusses Livatag, a nanoparticle formulation of doxorubicin (Transdrug technology) developed for the treatment of primary liver cancer.
by Peter Ciszewski | Nov 19, 2017
Sandesh Seth, Chairman and Chief Executive Officer of Actinium Pharmaceuticals, provides an update on its Actimab-A drug candidate in acute myeloid leukemia (AML). The Phase 2 trial is currently enrolling patients with AML age 60 and older who are unfit for standard...
