by Peter Ciszewski | Apr 24, 2020
Still’s disease is an inflammatory condition characterized by high fevers, rash, sore throat, and joint pain. As it progresses, adult-onset Still’s disease may lead to chronic arthritis and other complications. Still’s disease was named after an...
by Peter Ciszewski | Apr 24, 2020
Recently, we spoke to Beverley Francis-Gibson, President of the Sickle Cell Disease Association of America (SCDAA) about what her organization is doing to assist patients with sickle cell disease during the current COVID-19 pandemic. SCDAA is a non-profit organization...
by Peter Ciszewski | Apr 23, 2020
Dwight Koeberl, MD, PhD of Duke University School of Medicine explains the difference between enzyme replacement therapy (ERT) and gene therapy, as it relates to lysosomal storage disorders like Pompe disease. Dr. Koebel is currently conducting a gene therapy...
by Peter Ciszewski | Apr 22, 2020
Riam Shammaa, MD, Founder and CEO of INTELLiSTEM Technologies, talks about some of the hurdles his company has to overcome to develop a vaccine for COVID-19, during the lockdown. As Dr. Shammaa explains in this video, one of the more surprising problem they had...
by Peter Ciszewski | Apr 21, 2020
The U.S. Food and Drug Administration (FDA) has approved the kinase inhibitor, Pemazyre (pemigatinib), to treat adults with previously treated, unresectable locally advanced or metastatic cholangiocarcinoma with a fibroblast growth factor receptor 2 (FGFR2) fusion or...