by Peter Ciszewski | Feb 12, 2020
By Fran Sverdrup, PhD, Associate Professor, Department of Biochemistry and Molecular Biology at Saint Louis University. Facioscapulohumeral muscular dystrophy (FSHD) is one of the most common forms of muscular dystrophy. The name itself offers important insights...
by Peter Ciszewski | Feb 12, 2020
Ruth-Anne Langan Pai, PHD Candidate and the collaborative research project lead for the Castleman Disease Collaborative Network (CDCN) provides an overview of Castleman disease. Castleman disease is a group of rare disorders characterized by lymph node...
by Peter Ciszewski | Feb 11, 2020
James Dean, MD, senior medical director at Pharmacyclics provides an update on the most recent long-term data showing ibrutinib to be safe and effective for treating patients with chronic lymphatic leukemia (CLL). CLL is a rare blood cancer resulting in a...
by Peter Ciszewski | Feb 10, 2020
Eric T. Wong, MD, Associate Professor at Harvard Medical School provides an overview of rare cancers. Unlike rare diseases that are defined as affecting less than 200,000 people in the United States, rare cancers are referred to those affecting less than 45,000...
by Peter Ciszewski | Feb 7, 2020
On February 10 – 13, 2020, leading lysosomal disease researchers will come together to share the latest scientific information about rare lysosomal conditions at WORLDSymposium. The annual event provides an opportunity for basic, transitional, and clinical researchers...
