Advice for New SMA Parents

  Stacy Pokorny, a mother of a young girl with spinal muscular atrophy (SMA), gives advice to parents of children who have recently been diagnosed with the disease.  SMA is a rare inherited neuromuscular disorder caused by an inadequate level of the survivor...

Prader-Willi Syndrome: Overview and Potential Treatment

Rudolf Baumgartner, MD, Chief Medical Officer and Head of Clinical Development at Saniona, gives an overview of Prader-Willi syndrome (PWS) and tesomet, a drug combination under investigation for the treatment of PWS.   As Dr. Baumgartner explains, PWS is a rare...

Potential Treatment Option for Hepatorenal Syndrome

Florence Wong, MD, Hepatologist at Toronto General Hospital discusses terlipressin, a potent vasopressin analogue being investigated for the treatment of hepatorenal syndrome type 1 (HRS-1).     In the first part of the interview, Dr. Wong describes the...