by Peter Ciszewski | Sep 2, 2018
Greg Duncan, President and Chief Executive Officer of Celtaxsys, provides an overview of cystic fibrosis (CF), an inherited chronic disease that affects the lungs and digestive system of about 70,000 children and adults worldwide. Cystic fibrosis is caused by...
by Peter Ciszewski | Aug 30, 2018
Editor’s Note: This interview was conducted at #Bio2018. Please pardon the background noise. Barry Greene, President of Alnylam, discusses how his company works with advocacy groups in the diseases they are committed to.
by Peter Ciszewski | Aug 29, 2018
Jeremy Levin, Chairman and Chief Executive Officer of Ovid Therapeutics, discusses the challenges of a small biotech company working with rare diseases, especially rare neurological disorders.
by Peter Ciszewski | Aug 29, 2018
Pfizer announced positive data from it’s phase 3 study (called ATTR-ACT), which evaluated it’s experimental therapy Tafamidis (vyndaqel) in patients with wild-type or variant (hereditary) transthyretin amyloid cardiomyopathy (ATTR-CM). Tafamidis achieved...
by Peter Ciszewski | Aug 28, 2018
Openly Rare with Paul Kidwell is a monthly podcast series dedicated to the discussion around rare diseases. The podcast, created and hosted by Paul Kidwell, a 20-year PR veteran within the life science industry, will feature timely conversations with researchers,...
