by CheckRare Staff | Dec 1, 2022
Bonnie Smeryage, NP, Pediatric Nurse Practitioner in Hollywood, FL, discusses the benefits of liquid formulations in pediatric populations. Pediatric medication nonadherence is a major challenge for health care providers. Many patients do not take their...
by CheckRare Staff | Nov 28, 2022
Sean J. Pittock, MD, Director of Mayo Clinic’s Center for Multiple Sclerosis and Autoimmune Neurology and of Mayo’s Neuroimmunology Laboratory discusses the latest results from Phase III CHAMPION-NMOSD trial recently presented at European Committee...
by CheckRare Staff | Nov 15, 2022
Barry S. Ticho, MD, PhD, Chief Medical Officer at Stoke Therapeutics, discusses the phase 1/2a MONARCH study, which is evaluating STK-001 in patients with Dravet syndrome. As Dr. Ticho explains, Dravet syndrome is a rare neurological condition that usually...
by CheckRare Staff | Nov 8, 2022
Gustavo A. Heresi, MD, MS, Director of the Pulmonary Vascular and Chronic Thromboembolic Pulmonary Hypertension Program in the Department of Pulmonary and Critical Care Medicine in the Respiratory Institute at Cleveland Clinic discusses caring for patients with...
by CheckRare Staff | Nov 4, 2022
Alex Kolevzon, MD, Professor of Psychiatry and Pediatrics at the Icahn School of Medicine at Mount Sinai, explains the pathophysiology of Phelan-McDermid syndrome and how it is current treated. Phelan-McDermid syndrome is genetic disorder and one of few known...