by CheckRare Staff | Aug 28, 2023
Mary P. McGowan, MD, chief medical officer of the Family Heart Foundation provides an overview of homozygous familial hypercholesterolemia (HoFH). HoFH is a rare genetic disorder that results in severe impairment of the low-density lipoprotein receptor...
by CheckRare Staff | Aug 24, 2023
Richard Lafayette, MD, FACP, Director of the Stanford Glomerular Disease Center, and Rheumatologist at Stanford Health Care, describes the current standard of care for immunoglobulin A (IgA) nephropathy. IgA nephropathy (Berger’s disease) is a rare...
by CheckRare Staff | Aug 23, 2023
Binod Dhakal, MD, Associate Professor at Medical College of Wisconsin discusses results of the phase 3 multiple myeloma clincial trial. This trial compared Ciltacabtagene autoleucel to standard of care in patients with lenalidomide-refractory multiple myeloma. ...
by CheckRare Staff | Aug 22, 2023
Patrick Lewis, PharmD, Senior Director, Medical Affairs at Amryt Pharma discusses the latest data presented at ENDO 2023 on oral octreotide to treat acromegaly. Acromegaly is a rare endocrine disorder due to excess levels of growth hormone (GH). A benign...
by CheckRare Staff | Aug 21, 2023
Bob Lojewski, CSL Behring’s senior vice president and general manager of North America, talks about the changes in the treatment landscape for hemophilia B, including the recent use of gene therapy. Hemophilia B is a rare bleeding disorder caused by...
