by CheckRare Staff | Aug 22, 2023
Patrick Lewis, PharmD, Senior Director, Medical Affairs at Amryt Pharma discusses the latest data presented at ENDO 2023 on oral octreotide to treat acromegaly. Acromegaly is a rare endocrine disorder due to excess levels of growth hormone (GH). A benign...
by CheckRare Staff | Aug 21, 2023
Bob Lojewski, CSL Behring’s senior vice president and general manager of North America, talks about the changes in the treatment landscape for hemophilia B, including the recent use of gene therapy. Hemophilia B is a rare bleeding disorder caused by...
by CheckRare Staff | Aug 17, 2023
Patrick Lewis, PharmD, Senior Director, Medical Affairs at Amryt Pharma discusses the treatment options for patients with acromegaly. Acromegaly is a rare endocrine disorder due to excess levels of growth hormone (GH). In many cases, a benign...
by CheckRare Staff | Aug 15, 2023
Cary Harding, MD, at Oregon Health & Science University (OHSU), provides an overview of phenylketonuria (PKU). Toxic levels of the amino acid phenylalanine (Phe) cause PKU, a rare metabolic disease that can result in neurocognitive deficits....
by CheckRare Staff | Aug 14, 2023
Patrick Lewis, PharmD, Senior Director, Medical Affairs at Amryt Pharma provides an overview of acromegaly and why diagnostic delays for this rare disease are so common. Acromegaly is a rare endocrine disorder caused by excess levels of growth hormone...