by James Radke | Sep 16, 2020
The management of patients with Mucopolysaccharidosis I (MPS I) requires a team of health care professionals, from neurologists and orthopedic surgeons to pediatricians and genetic counselors. In this 4 module CME/CE program, hosted by Paul Orchard, MD from...
by James Radke | Sep 14, 2020
Nirmish Shah, MD, Director of the Sickle Cell Transition Program at Duke University talks about some of the strategies they employ to help patients with sickle cell disease and beta-thalassemia transition from pediatric to adult care. Dr. Shan noted that...
by James Radke | Sep 11, 2020
Amy Blum of the National Gaucher Foundation discusses the important role patient advocacy groups can play in helping the rare disease community during the current COVID-19 pandemic. This presentation was part of the live GRIDS 2020-Virtual Summit held July 1,...
by James Radke | Sep 9, 2020
Ryan Colburn, a man with late-onset Pompe disease talks about his personal perspective on the risk involved in managing his condition, job, and personal life during the pandemic. Pompe disease is a rare lysosomal disorder that can lead to a plethora of...
by James Radke | Sep 8, 2020
Cynthia Frank of the Gaucher Community Alliance discusses the important role patient advocacy groups can play in helping the rare disease community during the current COVID-19 pandemic. This presentation was part of the live GRIDS 2020-Virtual Summit held July...
