Pulmonary Arterial Hypertension Barriers

Shanna Martin, Registered Nurse from Shields Health Solutions, discusses common barriers clinicians face in managing patients with pulmonary arterial hypertension (PAH).   PAH is a rare, progressive disorder characterized by high blood pressure (hypertension) in...

Late-Stage Neuromuscular Disorders: MAiD

Akram Khan, MD, FCCP, Associate Professor of Pulmonary, Allergy, and Critical Care Medicine at Oregon Health & Science University, talks about medical assistance in dying (MAiD) regarding late-stage neuromuscular disorders.   Recently, the American College of...

Myasthenia Gravis and Targeted Therapies

Sindhu Ramchandren, MD, Global Clinical Leader at Janssen Pharmaceuticals, explains the pathophysiology of myasthenia gravis and the need for more targeted therapies.   Myasthenia gravis is an autoimmune, neuromuscular disorder characterized by weakness of the...

The LAVENDER Trial

  Ponni Subbiah, MD, MPH, Chief Medical Officer at Acadia Pharmaceuticals, discusses the results of the LAVENDER trial, which led to the approval of trofinetide (DAYBUE) in patients with Rett syndrome.   Rett Syndrom Background Rett syndrome is a rare...