GM1 Gangliosidosis Explained

Samiah Al-Zaidy, MD, Vice President of Clinical Development and Lead on the Passage Bio GM1 Gangliosidosis (GM1) Program, gives an overview of GM1.   As Dr. Al-Zaidy explains, GM1 is an inherited lysosomal disorder caused by mutations in the GLB1 gene. These...

Pulmonary Arterial Hypertension Barriers

Shanna Martin, Registered Nurse from Shields Health Solutions, discusses common barriers clinicians face in managing patients with pulmonary arterial hypertension (PAH).   PAH is a rare, progressive disorder characterized by high blood pressure (hypertension) in...

Late-Stage Neuromuscular Disorders: MAiD

Akram Khan, MD, FCCP, Associate Professor of Pulmonary, Allergy, and Critical Care Medicine at Oregon Health & Science University, talks about medical assistance in dying (MAiD) regarding late-stage neuromuscular disorders.   Recently, the American College of...

Myasthenia Gravis and Targeted Therapies

Sindhu Ramchandren, MD, Global Clinical Leader at Janssen Pharmaceuticals, explains the pathophysiology of myasthenia gravis and the need for more targeted therapies.   Myasthenia gravis is an autoimmune, neuromuscular disorder characterized by weakness of the...