by Madaline Spencer | Apr 3, 2025
Recent data details the results of treatment with botulinum toxin versus strabismus surgery for acute acquired concomitant esotropia (AACE). AACE is a rare, distinct subtype of esotropia. It is characterized by sudden onset of simultaneous esotropia, where the eyes...
by Madaline Spencer | Apr 2, 2025
Aravindhan Veerapandiyan, MD, Assistant Professor of Pediatrics, University of Arkansas and Arkansas Children’s Hospital, discusses results from the phase 1/2 EXPLORE44 clinical trial for Duchenne muscular dystrophy (DMD). DMD affects the muscles,...
by Madaline Spencer | Apr 1, 2025
The U.S. Food and Drug Administration (FDA) has approved Qfitlia (fitusiran) for the treatment of hemophilia A and B with or without inhibitors. Hemophilia is an inherited bleeding disorder in which the blood does not clot normally. People with the condition will...
by Madaline Spencer | Apr 1, 2025
The U.S. Food and Drug Administration (FDA) has approved Vykat XR (diazoxide choline), for the treatment of hyperphagia in patients four years of age and older with Prader-Willi syndrome (PWS). PWS is a rare genetic condition that affects many parts of the body but...
by Madaline Spencer | Mar 31, 2025
A recent study analyzed the incidence and characteristics of cutaneous squamous cell carcinoma (cSCC) in patients with Sézary syndrome. Sézary syndrome is a rare, aggressive form of cutaneous T-cell lymphoma (CTCL), a group of rare cancers that occur when T-cells...
