by Madaline Spencer | Jun 3, 2026
The US Food and Drug Administration (FDA) has approved pivekimab sunirine-pvzy for adults with blastic plasmacytoid dendritic cell neoplasm (BPDCN). BPDCN is a rare, aggressive CD4+ CD56+ myeloid cancer characterized by cutaneous lesions, bone marrow involvement, and...
by Madaline Spencer | Jun 3, 2026
Sumaira Ahmed, Founder and Executive Director of The Sumaira Foundation, discusses her organization and the BEST-NMOSD clinical trial for patients with neuromyelitis optica spectrum disorder (NMOSD). NMOSD is a rare autoimmune disorder that...
by Madaline Spencer | May 29, 2026
Logan Schneider, MD, Adjunct Clinical Associate Professor of Psychiatry and Behavioral Sciences at Stanford University, discusses the DUET clinical trial of Xywav (low sodium oxybate) in patients with narcolepsy. Narcolepsy is a chronic neurological...
by Madaline Spencer | May 28, 2026
Omar Sinno, MD, US Medical Strategy Lead for Rare Disease at UCB Pharma, discusses data presented on myasthenia gravis (MG) at the 2026 American Academy of Neurology meeting. MG is a chronic autoimmune neuromuscular disease characterized by weakness of...
by Madaline Spencer | May 26, 2026
Mauro Cives, MD, Associate Professor of Medical Oncology at the University of Bari, Italy, discusses the upcoming regulatory decision for LNTH-2501 to improve imaging of neuroendocrine tumors (NETs). NETs are rare tumors that usually develop in the...