by Madaline Spencer | Sep 9, 2026
The US Food and Drug Administration (FDA) has approved Zanvastro (zilganersen) for the treatment of pediatric and adult patients with Alexander disease. Alexander disease is a rare leukodystrophy that impairs neuronal signalling. Most cases of Alexander disease begin...
by Madaline Spencer | Sep 8, 2026
Neil Inhaber, MD, FRCPC, Therapeutic Area Head of Global Medical, Rare Disease at Takeda, discusses data on maribavir in post-transplant cytomegalovirus (CMV) presented at the American Transplant Congress 2026. Post-transplant CMV is one of the most common...
by Madaline Spencer | Sep 7, 2026
Christine Gustafson, Executive Director and CEO of the TED Community Organization, discusses the new Graves’ Community website. Graves’ disease is an autoimmune disease characterized by generalized overactivity of the thyroid gland. Thyroid eye disease...
by Madaline Spencer | Sep 4, 2026
Tammy Anderson, Executive Director, and Jenny Rose, Manager of Outreach and Management at Wake Up Narcolepsy, discuss the challenges of diagnosing narcolepsy and the profound impact the disorder can have on patients and their families. Both Ms. Anderson and Ms. Rose...
by Madaline Spencer | Sep 4, 2026
The US Food and Drug Administration (FDA) has approved Rasonque (daraxonrasib) for the treatment of adults with metastatic pancreatic adenocarcinoma (PDAC) who have received at least one prior systemic therapy or who are not candidates for multiagent systemic therapy....
