by CheckRare Staff | Feb 26, 2024
Tyler Sandahl, PharmD, Clinical Pharmacist at the Mayo Clinic, discusses the use of tocilizumab in multiple myeloma patients. Multiple myeloma is a cancer that occurs due to abnormal, uncontrolled growth of plasma cells in the bone marrow. The most...
by CheckRare Staff | Feb 23, 2024
February 29 Is Rare Disease Day! Rare Disease Day, observed on the last day of February every year, is a reminder of the challenges faced by those living with a rare disease. Established in 2008 by EURORDIS (The European Organisation for Rare Diseases),...
by CheckRare Staff | Feb 21, 2024
Davide Martino, MD, McMaster University Department of Medicine, discusses the BASIS clinical trial, a phase 3 study testing marstacimab in patients with hemophilia without inhibitors. Hemophilia is a bleeding disorder that slows the blood clotting...
by CheckRare Staff | Feb 19, 2024
Bernd Kasper, MD, PhD, Mannheim Cancer Center at University of Heidelberg in Germany, and Principal Investigator of the DeFi trial, discusses desmoid tumors and the approval of Ogsiveo (nirogacestat). A desmoid tumor is a benign, locally invasive...
by CheckRare Staff | Feb 17, 2024
Nicole Miller, PhD, Vice President of Molecular Diagnostics at Ultragenyx Pharmaceutics, explains the importance of improving newborn screening and the limitations of current processes. The Recommended Uniform Screening Panel (RUSP) is a list of...
