by CheckRare Staff | Sep 14, 2026
Fabry Disease: Patients’ Real-World Problems and How to Manage Them Staci Kallish, DO; Dawn Laney, MS, CGS, CCRC This educational program, hosted by Staci Kallish, DO, and Dawn Laney, MS, CGS, CCRC, examines how best to address patients’ real-life concerns...
by CheckRare Staff | Sep 9, 2026
In this episode of The CheckRare Brief, we discuss two recent FDA approvals for rare diseases, including Zanvastro for Alexander disease and Besremi for essential thrombocythemia (ET). We also examine a new gene therapy application for Huntington’s disease and...
by CheckRare Staff | Sep 9, 2026
For people living with rare endocrine disorders, getting an accurate diagnosis can be a long and frustrating journey. Symptoms may be subtle, overlap with more common conditions, or involve multiple organ systems, making it difficult for healthcare providers to...
by CheckRare Staff | Sep 3, 2026
In this episode of The CheckRare Brief, we discuss four recent FDA approvals, including LISRAYA for dermatomyositis and Imaavy for warm autoimmune hemolytic anemia (wAIHA), Mimrylo for polycythemia vera (PV), and Rasonque for pancreatic cancer. We also examine...
by CheckRare Staff | Sep 1, 2026
September is Narcolepsy Awareness Month, a time dedicated to increasing understanding of narcolepsy and supporting the individuals and families impacted by this rare neurological disorder. Narcolepsy is characterized by abnormal regulation of sleep-wake states and,...
