by Madaline Spencer | May 31, 2023
Sitra Tauscher-Wisniewski, MD, Vice President of Clinical Development & Analytics at Novartis Gene Therapies, discusses long-term data for onasemnogene abeparvovec (Zolgensma), an FDA-approved gene therapy for spinal muscular atrophy (SMA). SMA is a...
by Madaline Spencer and James Radke, PhD | May 30, 2023
Samiah Al-Zaidy, MD, Vice President of Clinical Development and Lead on the Passage Bio GM1 Gangliosidosis (GM1) Program, gives an overview of GM1. As Dr. Al-Zaidy explains, GM1 is an inherited lysosomal disorder caused by mutations in the GLB1 gene. These...
by Madaline Spencer and James Radke, PhD | May 24, 2023
Shanna Martin, Registered Nurse from Shields Health Solutions, discusses common barriers clinicians face in managing patients with pulmonary arterial hypertension (PAH). PAH is a rare, progressive disorder characterized by high blood pressure (hypertension) in...
by Madaline Spencer and James Radke, PhD | May 23, 2023
Akram Khan, MD, FCCP, Associate Professor of Pulmonary, Allergy, and Critical Care Medicine at Oregon Health & Science University, talks about medical assistance in dying (MAiD) regarding late-stage neuromuscular disorders. Recently, the American College of...
by Madaline Spencer and James Radke, PhD | May 22, 2023
Marc Rothenberg, MD, of the Consortium of Eosinophilic Gastrointestinal Disease Researchers (CEGIR), and Professor of Medicine at Cincinnati Children’s Hospital, gives an overview of the recent study showing removal of milk from the diet is as effective as stricter...
